Tiny Molecules Hold Big Promise for Treating Neurodegenerative Disease

Many neurodegenerative diseases lack effective treatments, but two new papers offer hope that a new therapeutic strategy might improve the lives of people who suffer from conditions like amyotrophic lateral sclerosis, or ALS. The strategy focuses on short stretches of synthetic DNA, called antisense oligonucleotides, which target a gene and block it from expressing the protein it encodes.Read the whole story at Bioengineering Today: Antisense Oligonucleotide Therapy.